CausalSentinel

Protein Dossier — AP4M1 (AP-4 complex subunit mu-1)

MR feasibility tier: A — Published pQTL-MR estimates exist for this protein (retrieved below - not computed here).

1. Published MR estimates (retrieved, not computed)

Outcome beta se p method nSNP cis/trans coloc
Diagnoses - main ICD10: H25 Senile cataract -0.00256 0.000839 0.00229 Inverse variance weighted 2 trans NA
Diagnoses - main ICD10: H25 Senile cataract -0.00256 0.000839 0.00229 Inverse variance weighted 2 trans NA
Diagnoses - main ICD10: I48 Atrial fibrillation and flutter -0.0029 0.00103 0.00506 Inverse variance weighted 2 trans NA
Diagnoses - main ICD10: I48 Atrial fibrillation and flutter -0.0029 0.00103 0.00506 Inverse variance weighted 2 trans NA
Transferrin 0.164 0.0591 0.00555 Wald ratio 1 trans NA
HOMA-B -0.0348 0.0126 0.00583 Inverse variance weighted 2 trans NA
HOMA-B -0.0348 0.0126 0.00583 Inverse variance weighted 2 trans NA
ER-negative Breast cancer (Combined Oncoarray; iCOGS; GWAS meta analysis) -0.124 0.0469 0.00802 Inverse variance weighted 2 trans NA
ER-negative Breast cancer (Combined Oncoarray; iCOGS; GWAS meta analysis) -0.124 0.0469 0.00802 Inverse variance weighted 2 trans NA
Diagnoses - main ICD10: R11 Nausea and vomiting 0.0015 0.000603 0.0128 Inverse variance weighted 2 trans NA
Diagnoses - main ICD10: R11 Nausea and vomiting 0.0015 0.000603 0.0128 Inverse variance weighted 2 trans NA
Age at menarche -0.0551 0.0228 0.0155 Inverse variance weighted 2 trans NA
…and 195 more outcomes (see JSON)              

2. pQTL instrument availability (Tier-B probe)

No prot-* pQTL GWAS dataset found for this protein (matched by UniProt accession and symbol).

3. GWAS Catalog results — traits with signal at this locus

9 association rows across 9 traits (8 genome-wide significant rows). Associations are loci, not causal claims; the mapped gene at a locus is not necessarily the effector gene.

Trait best p lead SNP n assoc study MR status
Circulating PILRB levels 2e-302 rs11766098 1 GCST90860357 no MR -> candidate analysis
Circulating PILRA levels 3e-231 rs11766098 1 GCST90860604 no MR -> candidate analysis
CNPY4 protein levels 7e-23 rs999885 1 GCST90468800 no MR -> candidate analysis
PILRB protein levels 2e-16 rs140843407 1 GCST90470237 no MR -> candidate analysis
PILRA protein levels 2e-15 rs140843407 1 GCST90470236 no MR -> candidate analysis
Mean corpuscular hemoglobin 1e-12 rs117460458 1 GCST007068 no MR -> candidate analysis
Hematological traits (multi-trait analysis) 1e-12 rs1534310 1 GCST90838663 no MR -> candidate analysis
Menarche (age at onset) 2e-8 rs999885 1 GCST007078 no MR -> candidate analysis
Alzheimer’s disease or family history of Alzheimer’s disease 5e-8 rs2293479 1 GCST005922 no MR -> candidate analysis

4. Phenome map — where this gene is a genetic locus, vs. where MR exists

Top diseases by Open Targets association (of 141 total). Associations are loci, not causal claims. The causal-status column is a four-state triage per pair: established (curated) = a curated clinical assertion exists (ClinGen/G2P/GEL/Orphanet/ClinVar — any validity level, MR adds little); exploratory rare-variant signal = ExWAS burden evidence without curation — a candidate NEW gene-disease relationship; common-variant locus = GWAS signal, classic pQTL-MR territory; multi-layer = burden+GWAS together, an allelic-series candidate (the strongest causal setup). Burden estimand is carrier-vs-noncarrier, not per-SD MR.

Disease genetic assoc. burden (ExWAS) causal status MR status
Severe intellectual disability and progressive spastic paraplegia 0.872 established (curated) no MR -> candidate analysis
Spastic paraplegia 0.94 established (curated) no MR -> candidate analysis
Intellectual disability 0.804 established (curated) no MR -> candidate analysis
hereditary disease 0.744 established (curated) no MR -> candidate analysis
AP-4 deficiency syndrome 0.52 established (curated) no MR -> candidate analysis
hereditary spastic paraplegia 0.676 established (curated) no MR -> candidate analysis
Abnormality of the nervous system 0.559 established (curated) no MR -> candidate analysis
microcephaly 0.426 established (curated) no MR -> candidate analysis
Global developmental delay 0.426 established (curated) no MR -> candidate analysis
Brain atrophy 0.426 established (curated) no MR -> candidate analysis
CNS hypomyelination 0.426 established (curated) no MR -> candidate analysis
Hypoplasia of the corpus callosum 0.426 established (curated) no MR -> candidate analysis
Alazami-Yuan syndrome 0.295 established (curated) no MR -> candidate analysis

Of the 13 rows above, 13 have no MR estimate in this resource. Across all retrieved diseases for this gene: 0 exploratory rare-variant signal(s), 0 multi-layer (allelic-series candidate) pair(s). Final triage still belongs to a statistical geneticist.

5. Downstream annotation (druggability & safety preview)

Layer Result
ChEMBL druggability not available — no ChEMBL target (undrugged)
gnomAD constraint pLI=8.2e-19, LOEUF=1.16 — LoF-tolerant
GWAS Catalog 98 unique SNPs / 196 rows
ClinVar 627 records; 10 pathogenic in sample of 30
PharmGKB/ClinPGx no annotations

Caveats declared by the tools

Sources

Provenance